Current Research
Improving Non-Viral Gene Transfer Agents
Assays
It is possible that only low levels of CFTR expression (in sufficient
numbers of appropriate cells) may be required to correct the basic CF
defect and that existing assays may not be sensitive enough to reliably
detect a level of CFTR gene transfer that may be clinically effective.
Hence we are putting substantial effort into both validating and
improving existing assays and developing more sensitive novel assays.
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